ScripRoche, Sarepta Therapeutics’ ex-US partner for the commercialization of Elevidys (delandistrogene moxeparvovec), has voluntarily and temporarily paused shipments of the Duchenne muscular dystrophy (DM
ScripThe deaths of two Duchenne muscular dystrophy (DMD) patients treated with the gene therapy Elevidys has moved beyond devastating the boys’ families and Sarepta Therapeutics’ stock price to shaking up
ScripThere have been numerous deals centered on metabolic dysfunction-associated steatohepatitis (MASH) over roughly the past decade, but the 14 May deal in which GSK acquired Boston Pharmaceuticals’ Phase
ScripThe first clinical data from CRISPR Therapeutics’ in vivo gene-editing candidate, CTX310, look promising, with steep drops in low-density lipoprotein (LDL)-cholesterol and triglyceride levels. The r