Orphaned No Longer: Big Pharma Embraces Drugs for Niche Markets

Hit hard by late stage pipeline failures and the regulatory and reimbursement challenges of traditional primary care products, Big Pharmas are taking renewed interest in drugs for orphan diseases, where high unmet medical need offers the promise of premium pricing and there's potential to grow the market via approval in multiple indications.

Jessica Merrill

Jeffery Kindler, CEO of Pfizer Inc., is surely a busy man. But back in December, he took time out of his schedule to address a diverse audience, made up...

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