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The Compelling Investment Case Of Rare Diseases

 
• By Arda Ural

Rare diseases are an underserved target for innovation, but development and commercialization hurdles can be staggering.  

Investment
• Source: Shutterstock

As we continue to see significant advancements in biotechnology innovation, many companies are increasingly shifting their focus to rare diseases — defined by the National Institutes of Health as conditions that impact fewer than 200,000 people in the US.

In total, there are approximately 7,000 to 10,000 known rare diseases, which collectively affect between 25 million and 30 million people across the country according to the NIH While these...

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