ScripAbout three months after reporting the first death of a Duchenne muscular dystrophy patient who received Elevidys (delandistrogene moxeparvovec), Sarepta Therapeutics reported on June 15 that a second
Pink SheetThe US Food and Drug Administration’s July advisory committee schedule includes a curious mix of vaccine safety reviews and the potentially triumphant return of a pulled multiple myeloma drug, in addi
Pink SheetSarepta Therapeutics is hoping to streamline development across its pipeline of gene therapies for limb-girdle muscular dystrophies thanks to a US Food and Drug Administration platform technology des
ScripThe latest readout of data from Regenxbio’s Phase I/II AFFINITY DUCHENNE study of its gene therapy RGX-202 in Duchenne muscular dystrophy (DMD) offers more support for the firm’s plan to seek US Food